ical and stem cell gene therapy 5) Established full R&D capabilities in San Diego AN OC arum CALIFOR111111 /TEM CELL ',Gene* 4 EFTA00292523 E-CELTM Clinical Development Focus on Transforming Olt. Hematology & Oncology 1. E-CEL Stem-Cell Gene Therapy • Goal: Cure genetic blood diseases(e.g., Sickle Cell Anemia)